Zandy Forbes’ biotech company MeiraGTx has developed targeted gene therapy methods to treat more than just genetic disorders.

Dina Anpilogova's concerns over her son's health were dismissed by doctors, so she took matters into her own hands.

She visited her son's pediatrician who referred the three-month-old to a children's hospital in Seattle where scans showed there were two tumors in Elijah's brain ... go blind or become paralyzed ...

Scientists in the UK have successfully used gene therapy to restore some vision to legally blind children with an inherited retinal condition. All 11 children in the clinical trial saw improvements ...

When you’re diagnosed with brain cancer, learning as much as you can about it can help you choose the best treatment for you. This guide shows you the basics on the types of brain cancer and how ...