ALS is autoimmune disease After years of research, finally a potential answer as to what causes ALS. Amyotrophic lateral ...

Partnership leverages AI-powered genome design to optimize AAV constructs, accelerate lead candidate selection, and improve drug substance manufacturability for rare and ultra-rare neuromuscular ...

Every movement we make, whether walking, speaking or even breathing, depends on the health of our muscles and nerves.

Robust improvement demonstrated across diverse set of clinical measures -- Patient-reported outcomes support clinical meaningfulness of ...

SAVANNAH, Georgia — Heart problems are common in the vast majority of neuromuscular disorders, and cardiac monitoring of patients is crucial, even at younger ages, a neurologist told an audience of ...

MLAB Biosciences, a biotechnology company pioneering novel therapies for neuromuscular disease, today announced the ...

Adeno-associated virus (AAV)–mediated gene therapy was one of the focal points of this year's Muscular Dystrophy Association conference. Here, Barry Byrne, MD, PhD, University of Florida, speaks to ...

SIOUX FALLS, S.D. (Dakota News Now) - Erin Darling knows firsthand what it’s like to live with a rare disease.

Dyne Therapeutics Inc. (NASDAQ:DYN) is one of the best stocks to buy under $20. On September 29, Dyne Therapeutics announced ...