Our inbox has been flooded with emails from viewers and readers who told us how their lives have been affected by rare ...
The Consolidated Appropriations Act of 2026, signed by Trump on Feb. 3, includes a provision reinstating the Mikaela Naylon ...
EVANSVILLE, Ind. (WEVV) — One-year-old Wrenley Lantaff is suffering from an extremely rare disease. Rajab interstitial is a ...
The Machesney Park resident estimates spending nearly $1000 per month on eye treatments to avoid irritation; one regimen ...
U.S. President Donald Trump signed a spending package into law Tuesday that reauthorizes the FDA’s previously stalled rare ...
The Senate failed to pass a massive spending bill on Thursday—which includes the rare pediatric PRV program but also funding ...
The author's son has hemophilia, a rare disorder requiring expensive, life-saving medication. The TrumpRx program aims to ...
For most teens, turning 16 means independence, driving, and new possibilities. For twin sisters Amelia and Makenzie Kahn, it ...
Feb 9 (Reuters) - Regenxbio said on Monday the U.S. Food and Drug Administration had declined to approve its gene therapy for ...
This Rare Disease Day, observed on Feb. 28 worldwide, the American Kidney Fund is committed to improving the understanding of ...
At Web Summit Qatar, AI-powered biotech startups describe how automation, data, and gene editing are filling labor gaps in ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results