A new, one-time treatment could be the answer to cure Huntington's disease, a neurodegenerative disease long-considered ...

Huntington’s disease is a hereditary condition that leads to the progressive degeneration of nerve cells (neurons) in specific areas of the brain. It mainly affects regions that control voluntary ...

Despite the best efforts of modern medicine, Huntington’s disease is a condition that still comes with a tragic prognosis.

Peake relates the story of folk music legend Woody Guthrie, "our greatest advocate," if only by accident. The ...

UCL and uniQure report the first treatment to slow Huntington’s disease with gene therapy AMT-130. High-dose patients had 75% less progression over three years compared with standard care. uniQure ...

May is Huntington's Disease Awareness Month, a time to bring national attention to a rare, hereditary, and relentlessly progressive brain disorder that affects entire families across generations. This ...

The path to approval for uniQure’s gene therapy candidate for Huntington’s disease is in doubt as the US Food and Drug Administration (FDA) has brought into question the adequacy of company’s Phase ...

Despite challenges like high therapy costs and regulatory hurdles, continuous R&D investments and strategic collaborations are fostering progress in personalized medicine, addressing critical unmet ...

May is Huntington’s Disease Awareness Month, a time to bring national attention to a rare, hereditary, and relentlessly progressive brain disorder that affects entire families across generations. This ...