Novartis secures FDA approval for Itvisma, a one-time gene therapy designed to boost motor function across a broad SMA ...
A new paper from the University of Kansas overturns the idea that a "risk gene" carried by millions of people worldwide ...
Technical advances allow researchers to trace the genetic changes that occur over time.
Cardiologist and Men's Health advisory board member Christopher Kelly, MD, says this treatment is "approaching magic" for ...
MedPage Today on MSN
FDA Gives Broad Approval to Gene Therapy for Rare Neurologic Disease
The FDA approved the intrathecal gene therapy onasemnogene abeparvovec (Itvisma) to treat spinal muscular atrophy (SMA) in ...
Oli-Jay Morris, two, was diagnosed with a unique gene mutation after he suffered involuntary movements shortly after birth - ...
Itvisma contains the active ingredient in Zolgensma approved in 2019 for children younger than 2 years but is reformulated for intrathecal administration across age groups.
1hon MSN
Missing the first mammogram linked to increased risk of breast cancer death, new study suggests
Women who miss their first screening appointment for breast cancer could have a 40% higher long-term risk of dying from the ...
A tot is the only known person in the world with a deadly condition after he was diagnosed when his left arm started shaking ...
A tot is the only known person in the world with a deadly condition after he was diagnosed when his left arm started shaking ...
The Food and Drug Administration granted accelerated approval on Wednesday for a new drug developed by researchers at the ...
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