Australian researchers warn GLP-1 weight-loss drugs may cause scurvy, the historic "pirate disease," due to poor nutrition ...
Disc Medicine said on Friday the U.S. Food and Drug Administration has declined to approve its drug to treat a rare genetic disorder.
Our inbox has been flooded with emails from viewers and readers who told us how their lives have been affected by rare ...
The author's son has hemophilia, a rare disorder requiring expensive, life-saving medication. The TrumpRx program aims to ...
Wisconsin Live Desk talks with the founder of EverythingALS ahead of rare disease day. Kate Spade Outlet has slashed a $359 ...
Feb 9 (Reuters) - Regenxbio said on Monday the U.S. Food and Drug Administration had declined to approve its gene therapy for ...
Faced with a life-threatening metabolic disease, KJ’s doctors at Children’s Hospital of Philadelphia sprinted to create a ...
3dOpinion
Opinion - A legislative win at last, but delays were costly for children with rare diseases
Overshadowed by Washington’s chaos, the moment was anything but quiet for the children with cancer and their families who had ...
The Durham biotech has filed for FDA approval in one rare disease and is advancing trials in two others. The health care ...
The FDA has rejected a rare blood disease candidate from Disc Medicine, a compound that been granted expedited review through ...
Rare diseases affect only a small number of people yet have become an attractive target for ASX healthcare companies. ... Read More The post ASX healthcare players focusing on rare diseases as ...
Even when promising clinical trials exist, and the FDA allows expanded access, rare disease patients like my granddaughter ...
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