Four years later, the Phams are searching for a cure after their son was diagnosed with a rare neurological disorder, hoping to raise funds for clinical trials. Heavy snow warning as 5 feet to strike: ...

In today’s healthcare landscape, rare disease patients face uncertainty and challenges accessing necessary therapies due to policy changes that affect insurance coverage.

The death comes as rattlesnakes are beginning to appear on trails across Orange County earlier in the season, according to outdoor enthusiasts and animal control officials.

Orphan drugs are forecast to surpass $400 billion in 2032 sales, driven by accelerating rare disease innovation despite regulatory volatility, pricing pressures, and capital competition from ...

Stanford Medicine pediatric hematologist Agnieszka Czechowicz, MD, Ph.D., has devoted her research career to improving ...

Allen completes second Ruck4Rare & pledges $1 million to ACD's Race for a Cure Every mile I ruck, every fundraiser, ...

This biotech specializes in precision therapies for rare genetic diseases, with a pipeline targeting oncology and hematology indications.

A new study from the Cary Institute found 10% of ticks sampled carried multiple pathogens, including those that cause Lyme and babesiosis.

Drivers across the U.S. could face unusual spring hazards this weekend as record warmth hits the East while strong winds ...

Scientists have long searched for simple ways to detect Alzheimer’s disease early. In recent years, a protein found in the ...

Frontotemporal dementia is a serious brain disorder that affects how people think, behave, and communicate. Although it is ...

The human brain is an extraordinary organ, but when its complex systems malfunction, the results can be deeply unsettling. Throughout medical history, researchers have documented rare psychological ...